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Furthermore, the results from the phase 1 trial are promising, but MZ-101 now needs to be tested in people with Pompe disease. Researchers are working towards starting a phase 2 trial. This aspect of What Is Pompe Disease Pompe Disease News plays a vital role in practical applications.
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Furthermore, this forward-thinking review describes the residual unmet needs of the disease, delineates various strategies being employed to address these needs and improve therapeutic outcomes, and summarizes the promising emerging therapies in development for Pompe disease. This aspect of What Is Pompe Disease Pompe Disease News plays a vital role in practical applications.
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Furthermore, pompe Disease Current State and Future Treatments - PubMed. This aspect of What Is Pompe Disease Pompe Disease News plays a vital role in practical applications.
Moreover, this forward-thinking review describes the residual unmet needs of the disease, delineates various strategies being employed to address these needs and improve therapeutic outcomes, and summarizes the promising emerging therapies in development for Pompe disease. This aspect of What Is Pompe Disease Pompe Disease News plays a vital role in practical applications.
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